By June Kinoshita | Executive Director and Chief Operating Officer
We have exciting news! Your donations have funded the first recovery of FSH muscular dystrophy tissue from a patient who had surgery last November. Among the labs that received the tissue is Fulcrum Therapeutics, a Cambridge, Massachusetts biotech that is working on treatments for FSHD. Using this muscle tissue, Fulcrum has developed FSHD primary muscle stem cells known as myoblasts which are capable of being expanded and cultured in their laboratories for many uses. Fulcrum will use these FSHD myoblasts for disease characterization and early drug discovery activities. The company would like to make these cell lines available for wider distribution to other researchers.
We now have nearly a dozen research labs that have applied to receive tissues through this registry, and many patients who have registered to donate tissue. With your continued support, we will be able to deliver their invaluable donated tissues to the world's leading FSHD researchers. Thank you!
You can read more about Fulcrum's work here.
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