The Most Precious Gift for Medical Research

by Facioscapulohumeral Society/FSH Society
Play Video
The Most Precious Gift for Medical Research
The Most Precious Gift for Medical Research
The Most Precious Gift for Medical Research

Project Report | Feb 13, 2018
Donated tissue used to make "muscle in a dish" for drug research

By June Kinoshita | Chief Strategic Programs Officer

A Fulcrum researcher at work.
A Fulcrum researcher at work.

Your generous support of our program to deliver muscle tissue from FSH muscular dystrophy patients to researchers has led to the development of an innovative "muscle in a dish" that is now being used for drug discovery. According to a report in Clinical Leader, Massachusetts-based biotech company Fulcrum Therapeutics “is using tissue donated from patients with facioscapulohumeral (FSH) muscular find a treatment. The tissue is used to create research models that look and respond much like natural human tissues.”

The article goes on to explain, “Since Fulcrum opened for business in 2016, it has built a relationship with the FSH Society, a patient advocacy group championing FSH drug development and clinical trials, as well as funding for research. The group has been critical in helping Fulcrum understand the patient community and develop clinical outcome targets that are meaningful to both patients and families.”

“In addition to helping Fulcrum connect with the patient community, the FSH Society has also worked to draft a tissue protocol for patient donations through the NDRI (National Disease Research Interchange). The FSH Society partnered with the NDRI to create a nationwide registry of individuals with FSH which has been integral in allowing the NDRI collaboration to occur.”

The article explains why primary muscle tissue donated by patients is critical for Fulcrum’s ability to develop a model system for drug testing.

We thank you sincerely for making this breakthrough possible through your support of our tissue donation program.

Read the full article: Tissue Modeling May Cut Clinical Trial Time


Share on Twitter Share on Facebook

About Project Reports

Project reports on GlobalGiving are posted directly to by Project Leaders as they are completed, generally every 3-4 months. To protect the integrity of these documents, GlobalGiving does not alter them; therefore you may find some language or formatting issues.

If you donate to this project or have donated to this project, you can recieve an email when this project posts a report. You can also subscribe for reports without donating.

Sign up for updates

Organization Information

Facioscapulohumeral Society/FSH Society

Location: Lexington, MA - USA
Facebook: Facebook Page
Twitter: @FSHSociety
June Kinoshita
Project Leader:
June Kinoshita
Lexington , MA United States

Funded Project!

Combined with other sources of funding, this project raised enough money to fund the outlined activities and is no longer accepting donations.

Still want to help?

Find another project in United States or in Physical Health that needs your help.
Find a Project

Learn more about GlobalGiving

Teenage Science Students
Vetting +
Due Diligence


Woman Holding a Gift Card
Gift Cards

Young Girl with a Bicycle

Get incredible stories, promotions, and matching offers in your inbox

WARNING: Javascript is currently disabled or is not available in your browser. GlobalGiving makes extensive use of Javascript and will not function properly with Javascript disabled. Please enable Javascript and refresh this page.